UK national cycling champion Tom Staniford suffers from an extremely rare genetic disease that went undiagnosed until nowFor years, Tom Staniford has defied the odds, becoming a national cycling champion in Great Britain despite a debilitating illnessNow, researchers have learned what's causing h

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Lexicon Pharmaceuticals, Inc., a biopharmaceutical company focused on discovering breakthrough treatments for human disease, announced today that John Northcott has joined the company as its vice president of marketing, commercial strategy, and operations. Mr. Northcott brings extensive commercial

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April Karmazyn-Wall, a six-month-old baby suffering from the extremely rare genetic disorder Emanuel syndrome, may soon be joining her parents at home in Wallsend, a town in North Tyneside, England, Chronicle Live reportsCaused by an extra chromosome called derivative 22 referred to as der(22), Em

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The worldwide orphan drug market is set to reach $127 billion by 2018, accounting for nearly 16 percent of total prescription drug sales, according to the recently released Orphan Drug Report 2013 from EvaluateTo better serve its clients' needs in regard to this growing segment of the pharmaceutic

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PROSPECT - When her son, Gene, was only a few days old, Cassandra Locklear said doctors labeled him with a foreboding prognosis: "failure to thriveThe muscles in his mouth were so weak that he couldn't suck a bottle, Locklear saidDoctors weren't sure what was wrong, and, without the ability to ge

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Roche announced that the Japanese Ministry of Health, Labour and Welfare has approved Avastin for the treatment of malignant glioma, including newly diagnosed glioblastoma in combination with radiotherapy and temozolomide chemotherapy, and as monotherapy for treatment of recurrent GBM and certain

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AbbVie announced preliminary results from a Phase I study of ABT-199/GDC-0199, an investigational BCL-2 (B-cell lymphoma 2) selective inhibitor, in patients with high-risk relapsed/refractory chronic lymphocytic leukemia (CLL), and in patients with relapsed/refractory non-Hodgkin's lymphoma (NHL).

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Desiccated thyroid extract (DTE), derived from crushed preparations of animal thyroid glands, is a safe and effective alternative to standard T4 therapy in hypothyroid patients, a new study finds. The results will be presented at The Endocrine Society's 95th Annual Meeting in San FranciscoIn adult

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Researchers have found that antibodies against the human papillomavirus (HPV) may help identify individuals who are at greatly increased risk of HPV-related cancer of the oropharynx, which is a portion of the throat that contains the tonsilsIn their study, at least 1 in 3 individuals with orophary

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Joseph Pidala, M.D., M.S., assistant member of the Blood and Bone Marrow Transplant and Immunology programs at Moffitt Cancer Center, and colleagues from the Chronic Graft-Versus-Host Disease Consortium have determined that certain gastrointestinal and liver-related types of chronic graft-versus-T

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